Reported Saturday, Agios Presents RISE UP Phase 3 Data At EHA 2026 Showing Mitapivat Achieves 40.6% Hemoglobin Response Rate And 41.1% Reduction In Transfusion Burden Versus Placebo In Sickle Cell Disease
Mitapivat demonstrated statistically significant improvement in hemoglobin response compared with placebo, with rapid onset and durable effects
New analyses showed patients in mitapivat arm had clinically meaningful reduction in transfusion burden compared with placebo
Patients in mitapivat arm who achieved hemoglobin response had clinically meaningful benefits across measures of sickle cell pain crises, fatigue, and other patient-reported outcomes
Mitapivat was well-tolerated, with a safety profile consistent with previous trials of mitapivat in sickle cell disease
Company to host investor conference call and webcast today at 9:00 a.m. ET (3:00 p.m. CEST)
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